NHS England will commission vonicog alfa for the treatment and prevention of bleeding in adults with von Willebrand disease in accordance with the criteria outlined in these documents.

Alglucosidase alfa is recommended as a not for routine commissioning treatment option for infantile-onset Pompe disease (IOPD) within the criteria set out in this document.

This policy document outlines the arrangements for funding of treatment for bleeding episodes in people with acquired haemophilia A.

Babies and toddlers with a rare and fatal genetic condition can now receive a life-saving treatment on the NHS for the first time. Sebelipase alfa (Kanuma®), an enzyme replacement therapy, will become the first treatment available on the NHS for Wolman disease, a condition which presents in babies and children under two years old. Following […]

Vestronidase alfa is recommended to be available as a routine commissioning as a treatment option for infants with MPS VII within the criteria set out in this document.

Children and adults with a rare inherited bone disease will be able to access a potentially life-enhancing drug, thanks to an innovative deal between NHS England, NICE and manufacturer Alexion. Hypophosphatasia (HPP) is a rare inherited bone condition that can appear any time from before birth to adulthood. In babies it is often fatal, and […]

People in England who suffer from the ultra-rare Morquio A syndrome should in future be able to access the only drug for their condition after a ground-breaking agreement was reached between NHS England and the manufacturer. NHS England has successfully negotiated a deal on elosulfase alfa (brand name Vimizim) with manufacturers BioMarin Pharma. The five […]

Children in England with a rare condition which leads to early death are set to receive treatment on the NHS, after the health service struck a deal with manufacturers. Young people with Batten Disease – an incurable illness which affects the nervous system, causing seizures, visual impairment, mobility loss and early death – will now […]

Stroke-reducing heart implants and a life changing surgical procedure for children with cerebral palsy are among a host of new treatments that will now be routinely available for thousands of patients on the NHS. The NHS announced its plan to provide the latest innovative treatments for patients, just days after it celebrated its 70th anniversary. Hundreds […]

A commissioning policy is a document that defines access to a service for a particular group of patients. A NICE Technology Appraisal Guideline on the same topic will replace, or be incorporated into, a commissioning policy as appropriate. These are important documents that are developed to ensure consistency in access to treatments nationwide. The following […]