A new daily pill for endometriosis has been approved for use on the NHS and could help over a thousand women in England every year manage the symptoms of the debilitating condition. The once-a-day pill, linzagolix, will soon be available for NHS patients in England who have had previous treatment for endometriosis, following approval by the National […]
Thousands of NHS patients in England with multiple sclerosis (MS) are set to benefit from a life-changing ‘take at home’ tablet, as the NHS becomes the first healthcare system in Europe to roll it out widely to patients with active disease. The tablet, cladribine, requires just 20 days of treatment spread over four years, providing […]
Hundreds of children with severe epilepsy will be able to benefit from a groundbreaking new treatment on the NHS that could significantly reduce their seizures, providing new hope for them and their families. The drug, fenfluramine, will be funded for NHS patients in England from today (Thursday 20 February) after the National Institute for Health […]
Hundreds of patients with a rare genetic condition that causes rickets and severe bone and dental problems can now receive a “life-changing” new therapy on the NHS in England. Targeted drug burosumab has been shown to help transform the lives of adults with an inherited condition that leads to low levels of the mineral phosphate […]
In response to the MHRA and NICE decisions on lecanemab, Professor Sir Stephen Powis, NHS National Medical Director, said: “The NHS now awaits a final decision from the National Institute for Health and Care Excellence that will look at the clinical benefits and cost-effectiveness of lecanemab and determine if it should be routinely offered by the […]
Thousands of patients with multiple sclerosis are to benefit from a new 10-minute injection on the NHS that can help slow the progression of disability while cutting their treatment time in hospital by over 90%. Around 9,000 patients in England currently receiving the drug ocrelizumab via an infusion can now be offered a jab that […]
Professor Sir Stephen Powis, NHS National Medical Director, said: “This transformative gene therapy is the first of its kind for haemophilia B patients on the NHS and has the potential to significantly improve the lives of hundreds of people by helping to reduce symptoms such as painful bleeds. “It is a one-time therapy that could […]
From today (Monday 22 January), thousands of people with sickle cell disorder and thalassaemia in England will have access a world-first ‘blood matching’ genetic test on the NHS to better match their blood transfusions, reducing the risk of side effects and offering more personalised care. The NHS today becomes the first healthcare system in the […]
Patients with severe inherited blood disorders will be offered stem cell transplants on the NHS that could cure their condition and help avoid life-long blood transfusions. Thalassaemia is a rare disorder that affects the production of haemoglobin in the blood, leading to severe anaemia and debilitating tiredness, with patients needing to have blood transfusions every […]
Babies and toddlers with a rare and fatal genetic condition can now receive a life-saving treatment on the NHS for the first time. Sebelipase alfa (Kanuma®), an enzyme replacement therapy, will become the first treatment available on the NHS for Wolman disease, a condition which presents in babies and children under two years old. Following […]