Hundreds of children are set to benefit from a ‘miracle’ treatment for cystic fibrosis, which has already changed the lives of thousands of people, the NHS has announced today. Patients here were some of the first in Europe to benefit from Kaftrio when NHS England secured a landmark deal in June 2020. Nine out of […]

The NHS is set to make a drug for the rare, debilitating disorder phenylketonuria (PKU) available to patients of all ages for the first time. A deal has been struck by the NHS to secure a non-branded ‘generic’ version of the drug, sapropterin dihydrochloride, for patients with the inherited condition, which means patients cannot eat […]

A life-changing drug that can improve mobility in children and adults with a rare genetic condition will be available on the NHS following a new commercial deal, chief executive Amanda Pritchard announced today. Risdiplam will be used to treat hundreds of patients a year with Spinal Muscular Atrophy (SMA), a rare and often fatal genetic […]

The first treatment for sickle cell disease in over 20 years will be rolled out to thousands of patients in England with life-saving benefits, the head of the NHS announced today. People with the condition endure severe pain during a ‘sickle cell crisis’ that can occur multiple times per year, often requiring hospital admission so […]

Genetic testing on the NHS will spot a rare form of diabetes in thousands of people unaware they are living with the disease, alongside a new training scheme for staff. The test being rolled out across England can also spot whether people have passed the affected gene on to their children, while the health service […]

Children in England are set to be the first in the world to be offered a cure for hepatitis C, as part of NHS plans to eradicate the disease entirely. More than 100 children have been identified for treatment, with hundreds more set to benefit in the coming months and years. Those aged 3 to […]

Thousands of lives will be saved thanks to more blood pressure checks in high street pharmacies, the NHS said today. Every NHS pharmacy in England will be able to provide the lifesaving checks to people aged 40 and over from October thanks to a new deal between pharmacies and the NHS. Over the next five […]

Thousands of cystic fibrosis patients in England have had their health drastically improved by a “miracle” treatment, allowing one to give birth to a baby, since the NHS made it available exactly one year ago today. In the past 12 months, NHS patients in England benefited from one of the fastest rollouts in the world […]

Every patient who needs kidney dialysis will benefit from free transport to and from vital hospital appointments, the NHS in England announced today. New rules will also come into place to make it simpler for other patients to get free transport, including those with long term conditions and mobility problems. After a full public consultation […]

An ‘artificial pancreas’ designed to revolutionise the life of people with Type 1 diabetes will be provided by the NHS, 100 years after the discovery of insulin, health service chief executive Sir Simon Stevens announced today. Speaking at NHS Confederation’s conference this morning, Sir Simon said that up to 1,000 patients will benefit from a […]