NHS patients with rare bone disease to benefit from potentially life-transforming drug due to “first of a kind” agreement between NHS England and the manufacturer
Children and adults with a rare inherited bone disease will be able to access a potentially life-enhancing drug, thanks to an innovative deal between NHS England, NICE and manufacturer Alexion. Hypophosphatasia (HPP) is a rare inherited bone condition that can appear any time from before birth to adulthood. In babies it is often fatal, and […]